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LOGO OF THE IX LACLSD COURSE

Day 4 - September 17

EVALUATION OF SCIENTIFIC ACTIVITIES
Choose from 1 (worst) to 5 (best) below according to your degree of satisfaction.

SESSION 8 - Chair: Paula Rozenfeld - 08:00 - 10:00

1 - NIEMANN PICK C AND OTHER LYSOSOMAL TRANSPORT DISEASES - Andrés Klein (Chile)
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2 - GM1 AND GM2 CEROID LIPOFUSCINOSES - Hernán Amartino (Argentina)
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3 - MLD, KRABBE AND OTHER LEUKODYSTROPHIES - Natalia Gomez-Ospina (USA/Colombia)
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SESSION 9 - Chair: Carlos Prada - 10:30 - 12:30

1 - INFLAMMATION AND LDs - Paula Rozenfeld (Argentina)
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2 - DRUG DEVELOPMENT PROCESS FROM BENCH TO PHARMACY - Guilherme Baldo (Brazil)
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3 - MODIFIER GENES IN LYSOSOMAL DISEASES - Andrés Klein (Chile)
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SESSION 10 - Chair: Andrés Klein - 14:00 - 16:00

1 - NEONATAL SCREENING FOR LDs - Carlos Prada (USA/Colombia)
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2 - DIAGNOSIS OF LDS IN THE MULTIOMIC ERA - Filippo Vairo (USA/Brazil)
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3 - WHAT AN EMERGING LSD SPECIALIST SHOULD UNDERSTAND? - Uma Ramaswami (UK), Gregory Pastores (UK), Raphael Schiffmann (USA), Joseph Muenzer (USA)
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