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LOGO OF THE IX LACLSD COURSE

Day 3 - September 16

EVALUATION OF SCIENTIFIC ACTIVITIES
Choose from 1 (worst) to 5 (best) below according to your degree of satisfaction.

SESSION 6 - Chair: Hernán Amartino - 08:00 - 10:00

1 - LABORATORY DIAGNOSIS OF MPS AND RELATED DISEASES - Francyne Kubaski (USA/Brazil)
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2 - TREATMENT FOR MPS AND RELATED DISEASES - Joseph Muenzer (USA)
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3 - HEMATOPOIETIC STEM CELL TRANSPLANTATION IN LDs - Carmem Bonfim (Brazil)
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SESSION 7 - Chair: Joseph Muenzer - 10:30 - 12:30

1 - CLINICAL ASPECTS, DIAGNOSIS AND MANAGEMENT OF FABRY - Uma Ramaswami (UK)
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2 - KEY QUESTIONS ON GAUCHER, FABRY AND POMPE DISEASE - Discussion led by Gregory Pastores
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3 - USE AND PITFALLS OF AI IN THE DIAGNOSIS AND TREATMENT OF THE LDs - Raphael Schiffmann (USA)
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